Start, switch and stop (triple-S) criteria for enzyme replacement therapy of late-onset Pompe disease: European Pompe Consortium recommendation update 2024

Benedikt Schoser*, Nadine A M E van der Beek, Alexander Broomfield, Esther Brusse, Jordi Diaz-Manera, Andreas Hahn, Thomas Hundsberger, Cornelia Kornblum, Michelle Kruijshaar, Pascal Laforet, Eugen Mengel, Tiziana Mongini, David Orlikowski, Giancarlo Parenti, W W M Pim Pijnappel, Mark Roberts, Thomas Scherer, Antonio Toscano, John Vissing, Johanna M P van den HoutPieter A van Doorn, Stephan Wenninger, Ans T van der Ploeg

*Corresponding author for this work

Fingerprint

Dive into the research topics of 'Start, switch and stop (triple-S) criteria for enzyme replacement therapy of late-onset Pompe disease: European Pompe Consortium recommendation update 2024'. Together they form a unique fingerprint.

Keyphrases

Medicine and Dentistry