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Interim Results from a Dose Escalating Study of AMT-060 (AAV5-hFIX) Gene Transfer in Adult Patients with Severe Hemophilia BInterim Results from a Dose Escalating Study of AMT-060 (AAV5-hFIX) Gene Transfer in Adult Patients with Severe Hemophilia B

Frank W.G. Leebeek, Marco Tangelder, Karina Meijer, Giancarlo Castaman, Federica Cattaneo, Michiel Coppens, Peter Kampmann, Robert Klamroth, Roger E.G Schutgens, Erhard Seifried, Joachim Schwaeble, Halvard Boenig, Maaike Hendriks, Deya Corzo , Wolfgang A. Miesbach

    Original languageEnglish
    JournalBlood
    Volume128
    Pages (from-to)2314
    ISSN0006-4971
    Publication statusPublished - 2016

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