Functional Outcome Measures to Optimize Drug Development in Spinal and Bulbar Muscular Atrophy: Results From a Meta-Analysis of the Global SBMA Dataset

Spencer B Huggett, Andrew T N Tebbenkamp, Carlo Rinaldi, Dipa Jayaseelan, Luca Zampedri, Lorenzo Blasi, Andrea Fortuna, Abdullah Alqahtani, Angela Kokkinis, Julia Dahlqvist, Silvia Fenu, Eleonora Cavalca, Alessandro Bertini, Caterina Mariotti, Christopher Grunseich, Takahiro Kawase, Yoshiyuki Kishimoto, Shinichiro Yamada, Masahisa Katsuno, Pietro FrattaAmelia Conte, Mario Sabatelli, Gianni Soraru, John Vissing, Minsung Kang, Jin-Sung Park, Davide Pareyson, Vissia VigliettaShow 8 moreShow less