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Keyphrases
Hereditary Spastic Paraplegia
100%
Axonal Degeneration
100%
Chenodeoxycholic Acid
100%
Human Induced Pluripotent Stem Cell-derived Neurons
100%
Cerebrotendinous Xanthomatosis
100%
Induced Pluripotent Stem Cells (iPSCs)
57%
CYP7B1
57%
Cortical Projection Neurons
57%
Disease Mechanisms
28%
Axon
28%
Cell-based
28%
Disease-specific
28%
Stem Cell-derived
28%
Biochemical Alterations
28%
Novel Treatments
14%
Pharmacotherapy
14%
New Disease
14%
Disease-related
14%
Cholesterol
14%
Therapeutic Target
14%
Rare Diseases
14%
CYP27A1
14%
Human Embryonic Stem Cells (hESCs)
14%
Diseases Therapeutic
14%
Gene Regulating
14%
Fibroblast Cells
14%
Pluripotency Factors
14%
Pathogenic Mechanism
14%
Underlying Disease
14%
Skin Fibroblasts
14%
Bile Acids
14%
Bile Acid Metabolism
14%
Neurofilament
14%
Biochemical Changes
14%
Gene Deficiency
14%
Cause-effect Relationship
14%
Biallelic mutations
14%
Pluripotent
14%
Human Embryonic Stem Cell Lines
14%
Lipid Disturbances
14%
Critical Genes
14%
Gene Editing
14%
Episomal Vector
14%
Specific Lipids
14%
Cas9 Protein
14%
Vesiculation
14%
Corticospinal Motor Neurons
14%
Axonopathy
14%
Hereditary Spastic Paraplegia Type 5
14%
Pathogenic Strategy
14%
Neuronal Model
14%
Patient-specific iPSCs
14%
Medicine and Dentistry
Spastic Paraplegia
100%
Nerve Fiber Degeneration
100%
Induced Pluripotent Stem Cell
100%
Chenodeoxycholic Acid
100%
Cerebrotendinous Xanthomatosis
100%
Disease
85%
Axon
28%
Human Embryonic Stem Cell
28%
Drug Therapy
14%
Fibroblast
14%
Rare Disease
14%
CYP27A1
14%
DeJerine-Sottas Disease
14%
Bile Acid
14%
Bile Acid Metabolism
14%
Neurofilament
14%
Neuropathy
14%
Stem Cell Line
14%
Skin Fibroblast
14%
Cas9
14%
Clustered Regularly Interspaced Short Palindromic Repeat
14%
Human Pluripotent Stem Cell
14%
Neuroscience
Paraplegia
100%
Nerve Fiber Degeneration
100%
Axonal Degeneration
100%
Stem Cell
100%
Chenodeoxycholic Acid
100%
Axon
28%
Fibroblast
28%
Embryonic Stem Cell
28%
Bile Acid
28%
Cell Line
14%
Metabolic Pathway
14%
Hereditary Spastic Paraplegia
14%
Neurofilament
14%
Motor Neuron
14%
CRISPR
14%
Cholestanetriol 26 Monooxygenase
14%
Biochemistry, Genetics and Molecular Biology
Nerve Fiber Degeneration
100%
Induced Pluripotent Stem Cell
100%
Chenodeoxycholic Acid
100%
CYP7B1
57%
Fibroblast
28%
Axon
28%
Embryonic Stem Cell
28%
Lipid
14%
Stem Cell
14%
CYP27A1
14%
Bile Acid
14%
Bile Acid Metabolism
14%
Neurofilament
14%
Motor Neuron
14%
Stem Cell Line
14%
Genome Editing
14%
CRISPR/Cas9
14%