Safety of switching to Migalastat from enzyme replacement therapy in Fabry disease: Experience from the Phase 3 ATTRACT study

Derralynn A Hughes, Kathleen Nicholls, Gere Sunder-Plassmann, Ana Jovanovic, Ulla Feldt-Rasmussen, Raphael Schiffmann, Robert Giugliani, Vipul Jain, Chris Viereck, Jeffrey P Castelli, Nina Skuban, Jay A Barth, Daniel G Bichet

    14 Citationer (Scopus)
    OriginalsprogEngelsk
    TidsskriftAmerican Journal of Medical Genetics. Part A
    Vol/bind179
    Udgave nummer6
    Sider (fra-til)1069-1073
    Antal sider5
    ISSN1552-4825
    DOI
    StatusUdgivet - 1 jun. 2019

    Citationsformater