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Extremely hypomorphic and severe deep intronic variants in the ABCA4 locus result in varying Stargardt disease phenotypes

  • Jana Zernant
  • , Winston Lee
  • , Takayuki Nagasaki
  • , Frederick T Collison
  • , Gerald A Fishman
  • , Mette Bertelsen
  • , Thomas Rosenberg
  • , Peter Gouras
  • , Stephen H Tsang
  • , Rando Allikmets
67 Citationer (Scopus)

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Biochemistry, Genetics and Molecular Biology