Designing a single-arm phase 2 clinical trial of mitapivat for adult patients with erythrocyte membranopathies (SATISFY): a framework for interventional trials in rare anaemias - pilot study protocol

Andreas Glenthøj*, Eduard J van Beers, Richard van Wijk, Minke A E Rab, Evelyn Groot, Niels Vejlstrup, Nina Toft, Selma Kofoed Bendtsen, Jesper Petersen, Jens Helby, Fatiha Chermat, Pierre Fenaux, Kevin H M Kuo

*Corresponding author af dette arbejde

Fingeraftryk

Dyk ned i forskningsemnerne om 'Designing a single-arm phase 2 clinical trial of mitapivat for adult patients with erythrocyte membranopathies (SATISFY): a framework for interventional trials in rare anaemias - pilot study protocol'. Sammen danner de et unikt fingeraftryk.

Keyphrases

Pharmacology, Toxicology and Pharmaceutical Science

Medicine and Dentistry