Agalsidase beta treatment is associated with improved quality of life in patients with Fabry disease: findings from the Fabry Registry

Torquil Watt, Alessandro P Burlina, Chiara Cazzorla, Dorothee Schönfeld, Maryam Banikazemi, Robert J Hopkin, Ana Maria Martins, Katherine Sims, Dana Beitner-Johnson, Fanny O'Brien, Ulla Feldt-Rasmussen

    59 Citationer (Scopus)

    Abstrakt

    To evaluate the effect of agalsidase beta on longitudinal health-related quality of life in patients with Fabry disease.
    OriginalsprogEngelsk
    TidsskriftJournal of Endodontics
    Vol/bind12
    Udgave nummer11
    Sider (fra-til)703-12
    Antal sider10
    ISSN0099-2399
    DOI
    StatusUdgivet - 1 nov. 2010

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