Seneste publikationer Vis alle (29) »

1. Udgivet

   Safety, tolerability, pharmacokinetics, pharmacodynamics, and exploratory efficacy of the novel enzyme replacement therapy avalglucosidase alfa (neoGAA) in treatment-naïve and alglucosidase alfa-treated patients with late-onset Pompe disease: A phase 1, open-label, multicenter, multinational, ascending dose study

   Publikation: Bidrag til tidsskrift › Tidsskriftartikel › Forskning › peer review

2. Udgivet

   229th ENMC international workshop: Limb girdle muscular dystrophies - Nomenclature and reformed classification Naarden, the Netherlands, 17-19 March 2017

   Publikation: Bidrag til tidsskrift › Tidsskriftartikel › Forskning › peer review

3. Udgivet

   233rd ENMC International Workshop: Clinical Trial Readiness for Calpainopathies, Naarden, The Netherlands, 15-17 September 2017

   Publikation: Bidrag til tidsskrift › Tidsskriftartikel › Forskning › peer review